Hemoglobin S beta zero thalassemia
Showing 1 - 25 of >10,000
Mitapivat in Subjects With Sickle Cell Disease
Enrolling by invitation
- Sickle Cell Anemia
- +7 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Feb 2, 2023
Sickle Cell Disease, Hb-SS Disease, Hemoglobin S Trial run by the National Heart, Lung, and Blood Institute (NHLBI)
Not yet recruiting
- Sickle Cell Disease
- +5 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jun 21, 2023
Sickle Cell Disease, Sickle Beta Zero Thalassemia, Sickle B+ Thalassemia Trial in Chicago (MED-Go App)
Recruiting
- Sickle Cell Disease
- +3 more
- MED-Go App
-
Chicago, IllinoisAnn & Robert H Lurie Children's Hospital of Chicago
Mar 7, 2022
Thalassemia, Beta Trial in Karachi (hydroxyurea and thalidomide)
Completed
- Thalassemia, Beta
- hydroxyurea and thalidomide
-
Karachi, Sindh, PakistanChildren's Hospital Karachi
Nov 11, 2021
Sickle Cell Disease, Sickle B+ Thalassemia, Sickle Beta Zero Thalassemia Trial in Chicago (HU-Go app)
Completed
- Sickle Cell Disease
- +3 more
- HU-Go app
-
Chicago, IllinoisAnn & Robert H Lurie Children's Hospital of Chicago
Jul 27, 2021
Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)
Recruiting
- Beta-Thalassemia
- Sirolimus 0.5 mg
-
Ferrara, FE, Italy
- +3 more
Nov 11, 2021
Pulmonary Hypertension (PAH) in Patients With Thalassemia
Completed
- Thalassemia Major
- +2 more
- Physician standard-of-care according to ESC/ERS Guidelines
-
Orbassano, Turin, Italy
- +7 more
Aug 3, 2022
Thalassemia Trial in Worldwide (Luspatercept, Placebo, Best Supportive Care (BSC))
Active, not recruiting
- Thalassemia
- Luspatercept
- +2 more
-
Los Angeles, California
- +16 more
Aug 16, 2022
Sickle Cell Disease, Sickle-Beta Zero Thalassemia Trial in Brooklyn (SCD-101)
Recruiting
- Sickle Cell Disease
- Sickle-Beta Zero Thalassemia
-
Brooklyn, New YorkKing's County Hospital
Feb 19, 2021
Sickle Cell Disease, Sickle Cell Hemoglobin C, Sickle Beta Zero Thalassemia Trial in Chicago (PROs assessment using sickle cell
Completed
- Sickle Cell Disease
- +3 more
- PROs assessment using sickle cell disease mobile app (SCD-app)
-
Chicago, IllinoisAnn & Robert H. Lurie Children's Hospital of Chicago
Dec 17, 2020
Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)
Completed
- Transfusion-dependent Beta-Thalassemia
-
Peshawar, Khyber Pakhtunkhwa, PakistanBlood Care Clinic
Nov 19, 2023
Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)
Completed
- Thalassemia, Beta
- Hydroxyurea and Thalidomide
-
Karachi, Sindh, PakistanChildren's Hospital Karachi
Nov 23, 2023
Erythrocyte Transfusion, Beta-Thalassemia Trial in Worldwide (Luspatercept, Placebo)
Completed
- Erythrocyte Transfusion
- Beta-Thalassemia
- Luspatercept
- Placebo
-
Los Angeles, California
- +72 more
Jan 21, 2022
Sickle Cell Disease and Genomic and Gene Therapy Needs of
Recruiting
- Sickle Cell Disease
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Apr 4, 2022
Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)
Recruiting
- Transfusion Dependent Beta Thalassemia
- +3 more
- EDIT-301
-
Oakland, California
- +3 more
Jan 3, 2023
Frequency of COVID-19 Antibodies in Hereditary Hematological
Completed
- Thalassemia Major
- Covid19
- SARS-CoV-2 S1/S2 IgG
-
Monza, MB, ItalyASST Monza - Ospedale San Gerardo
Nov 6, 2020
Quality of Life in Thalassemic Patients at Assiut University
Not yet recruiting
- Thalassemia
- Abdominal ultrasound
- (no location specified)
Mar 17, 2023
Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia
Not yet recruiting
- Sickle Cell Disease, Beta Thalassemia Intermedia
- RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
- (no location specified)
May 30, 2023
Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))
Completed
- Beta Thalassemia Major
- Beta Thalassemia Intermedia
- SOTATERCEPT (ACE-011)
-
Créteil, France
- +14 more
Aug 18, 2022
ß-thalassemia Trial (BD211)
Not yet recruiting
- β-thalassemia
- BD211
- (no location specified)
Mar 15, 2023
Transfusion-dependent Beta-thalassemia After Gene Therapy
Recruiting
- Transfusion-dependent Beta-Thalassemia
- Gene Therapy
- Gene therapy
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Aug 6, 2023
Sickle Cell Disease, Sickle Cell Trait, Beta-Thalassemia Trial (High performance liquid chromatography, Automated sickling test,
Not yet recruiting
- Sickle Cell Disease
- +4 more
- High performance liquid chromatography
- +5 more
- (no location specified)
Aug 17, 2022
Transfusion-dependent Thalassemia Trial in Dhaka (Thalidomide Capsules, Placebo)
Recruiting
- Transfusion-dependent Thalassemia
- Thalidomide Capsules
- Placebo
-
Dhaka, BangladeshBangabandhu Sheikh Mujib Medical University
Oct 18, 2023
Beta-Thalassemia Trial (CS-101 injection)
Not yet recruiting
- Beta-Thalassemia
- CS-101 injection
- (no location specified)
Sep 27, 2023