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Hemoglobin S beta zero thalassemia

Showing 1 - 25 of >10,000

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Mitapivat in Subjects With Sickle Cell Disease

Enrolling by invitation
  • Sickle Cell Anemia
  • +7 more
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Feb 2, 2023

    Sickle Cell Disease, Hb-SS Disease, Hemoglobin S Trial run by the National Heart, Lung, and Blood Institute (NHLBI)

    Not yet recruiting
    • Sickle Cell Disease
    • +5 more
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jun 21, 2023

    Sickle Cell Disease, Sickle Beta Zero Thalassemia, Sickle B+ Thalassemia Trial in Chicago (MED-Go App)

    Recruiting
    • Sickle Cell Disease
    • +3 more
    • MED-Go App
    • Chicago, Illinois
      Ann & Robert H Lurie Children's Hospital of Chicago
    Mar 7, 2022

    Thalassemia, Beta Trial in Karachi (hydroxyurea and thalidomide)

    Completed
    • Thalassemia, Beta
    • hydroxyurea and thalidomide
    • Karachi, Sindh, Pakistan
      Children's Hospital Karachi
    Nov 11, 2021

    Sickle Cell Disease, Sickle B+ Thalassemia, Sickle Beta Zero Thalassemia Trial in Chicago (HU-Go app)

    Completed
    • Sickle Cell Disease
    • +3 more
    • HU-Go app
    • Chicago, Illinois
      Ann & Robert H Lurie Children's Hospital of Chicago
    Jul 27, 2021

    Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)

    Recruiting
    • Beta-Thalassemia
    • Sirolimus 0.5 mg
    • Ferrara, FE, Italy
    • +3 more
    Nov 11, 2021

    Pulmonary Hypertension (PAH) in Patients With Thalassemia

    Completed
    • Thalassemia Major
    • +2 more
    • Physician standard-of-care according to ESC/ERS Guidelines
    • Orbassano, Turin, Italy
    • +7 more
    Aug 3, 2022

    Thalassemia Trial in Worldwide (Luspatercept, Placebo, Best Supportive Care (BSC))

    Active, not recruiting
    • Thalassemia
    • Los Angeles, California
    • +16 more
    Aug 16, 2022

    Sickle Cell Disease, Sickle-Beta Zero Thalassemia Trial in Brooklyn (SCD-101)

    Recruiting
    • Sickle Cell Disease
    • Sickle-Beta Zero Thalassemia
    • Brooklyn, New York
      King's County Hospital
    Feb 19, 2021

    Sickle Cell Disease, Sickle Cell Hemoglobin C, Sickle Beta Zero Thalassemia Trial in Chicago (PROs assessment using sickle cell

    Completed
    • Sickle Cell Disease
    • +3 more
    • PROs assessment using sickle cell disease mobile app (SCD-app)
    • Chicago, Illinois
      Ann & Robert H. Lurie Children's Hospital of Chicago
    Dec 17, 2020

    Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)

    Completed
    • Transfusion-dependent Beta-Thalassemia
    • Peshawar, Khyber Pakhtunkhwa, Pakistan
      Blood Care Clinic
    Nov 19, 2023

    Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)

    Completed
    • Thalassemia, Beta
    • Hydroxyurea and Thalidomide
    • Karachi, Sindh, Pakistan
      Children's Hospital Karachi
    Nov 23, 2023

    Erythrocyte Transfusion, Beta-Thalassemia Trial in Worldwide (Luspatercept, Placebo)

    Completed
    • Erythrocyte Transfusion
    • Beta-Thalassemia
    • Los Angeles, California
    • +72 more
    Jan 21, 2022

    Sickle Cell Disease and Genomic and Gene Therapy Needs of

    Recruiting
    • Sickle Cell Disease
      • Memphis, Tennessee
        St. Jude Children's Research Hospital
      Apr 4, 2022

      Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

      Recruiting
      • Transfusion Dependent Beta Thalassemia
      • +3 more
      • EDIT-301
      • Oakland, California
      • +3 more
      Jan 3, 2023

      Frequency of COVID-19 Antibodies in Hereditary Hematological

      Completed
      • Thalassemia Major
      • Covid19
      • SARS-CoV-2 S1/S2 IgG
      • Monza, MB, Italy
        ASST Monza - Ospedale San Gerardo
      Nov 6, 2020

      Quality of Life in Thalassemic Patients at Assiut University

      Not yet recruiting
      • Thalassemia
      • Abdominal ultrasound
      • (no location specified)
      Mar 17, 2023

      Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia

      Not yet recruiting
      • Sickle Cell Disease, Beta Thalassemia Intermedia
      • RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
      • (no location specified)
      May 30, 2023

      Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))

      Completed
      • Beta Thalassemia Major
      • Beta Thalassemia Intermedia
      • SOTATERCEPT (ACE-011)
      • Créteil, France
      • +14 more
      Aug 18, 2022

      ß-thalassemia Trial (BD211)

      Not yet recruiting
      • β-thalassemia
      • BD211
      • (no location specified)
      Mar 15, 2023

      Transfusion-dependent Beta-thalassemia After Gene Therapy

      Recruiting
      • Transfusion-dependent Beta-Thalassemia
      • Gene Therapy
      • Gene therapy
      • Tianjin, Tianjin, China
        Regenerative Medicine Center
      Aug 6, 2023

      Sickle Cell Disease, Sickle Cell Trait, Beta-Thalassemia Trial (High performance liquid chromatography, Automated sickling test,

      Not yet recruiting
      • Sickle Cell Disease
      • +4 more
      • High performance liquid chromatography
      • +5 more
      • (no location specified)
      Aug 17, 2022

      Transfusion-dependent Thalassemia Trial in Dhaka (Thalidomide Capsules, Placebo)

      Recruiting
      • Transfusion-dependent Thalassemia
      • Thalidomide Capsules
      • Placebo
      • Dhaka, Bangladesh
        Bangabandhu Sheikh Mujib Medical University
      Oct 18, 2023

      Beta-Thalassemia Trial (CS-101 injection)

      Not yet recruiting
      • Beta-Thalassemia
      • CS-101 injection
      • (no location specified)
      Sep 27, 2023